ABBVIE | thyroid | Metabolic Disorders |
ABEONA | rebisufligene etisparvovec | Metabolic Disorders |
ACER THERAPEUTICS | OLPRUVA | Metabolic Disorders |
AEGERION PHARMACEUTICALS | MYALEPTA | Metabolic Disorders |
AEGLEA BIOTHERAPEUTICS | pegzilarginase | Metabolic Disorders |
AGIOS PHARMACEUTICALS | mitapivat | Metabolic Disorders |
ALBIREO PHARMACEUTICALS | odevixibat | Metabolic Disorders |
ALEXION PHARMACEUTICALS | KANUMA * | Metabolic Disorders |
ALNYLAM PHARMACEUTICALS | OXLUMO * | Metabolic Disorders |
ALTIMMUNE | pemvidutide | Metabolic Disorders |
ALTIMMUNE | pemvidutide | Metabolic Disorders |
APPLIED THERAPEUTICS | govorestat | Metabolic Disorders |
APTABIO THERAPEUTICS | isuzinaxib | Metabolic Disorders |
ASCENDIS PHARMA | lonapegsomatropin | Metabolic Disorders |
ASCENDIS PHARMA | palopegteriparatide | Metabolic Disorders |
ASTELLAS | zocaglusagene nuzaparvovec | Metabolic Disorders |
AVROBIO | voxeralgagene autotemcel | Metabolic Disorders |
BASF AGRICULTURE | icosabutate | Metabolic Disorders |
BIOMARIN | domofenogene zalfaparvovec | Metabolic Disorders |
BIOMARIN | pegvaliase | Metabolic Disorders |
BIOMARIN | reveglucosidase alfa | Metabolic Disorders |
BIOMARIN | tralesinidase alfa | Metabolic Disorders |
CATABASIS PHARMACEUTICALS | edasalonexent | Metabolic Disorders |
CATABASIS PHARMACEUTICALS | nicodicosapent | Metabolic Disorders |
CERECOR | demannose | Metabolic Disorders |
CERECOR | elfucose | Metabolic Disorders |
COHERUS BIOSCIENCES | ibrigampar | Metabolic Disorders |
CORCEPT THERAPEUTICS | miricorilant | Metabolic Disorders |
CORCEPT THERAPEUTICS | nenocorilant | Metabolic Disorders |
CORCEPT THERAPEUTICS | relacorilant | Metabolic Disorders |
DAEWOONG PHARMACEUTICALS | enavogliflozin | Metabolic Disorders |
DR. FALK PHARMA | norucholic acid | Metabolic Disorders |
DURECT | larsucosterol | Metabolic Disorders |
DURECT | larsucosterol | Metabolic disorders |
DURECT | larsucosterol sodium | Metabolic disorders |
ENYO PHARMA | vonafexor | Metabolic Disorders |
FERRING PHARMACEUTICALS | apraglutide | Metabolic Disorders |
FRESENIUS KABI | ADDNUTRIV * | Metabolic Disorders |
GALECTO BIOTECH | selvigaltin | Metabolic Disorders |
GALECTO BIOTECH | selvigaltin | Metabolic Disorders |
GALMED PHARMACEUTICALS | icomidocholic acid | Metabolic Disorders |
GENEXINE | eftansomatropin alfa | Metabolic Disorders |
GILEAD | cilofexor | Metabolic Disorders |
GILEAD | firsocostat | Metabolic Disorders |
GSK | linerixibat | Metabolic Disorders |
HIGHTIDE THERAPEUTICS | berberine ursodeoxycholate | Metabolic Disorders |
IBSA INSTITUT BIOCHIMIQUE | TIROSINT * | Metabolic disorders |
INVERSAGO PHARMA | zevaquenabant | Metabolic Disorders |
KADMON | CLOVIQUE | Metabolic Disorders |
KALEIDO BIOSCIENCES | onterodrimer | Metabolic Disorders |
LOGICBIO THERAPEUTICS | alvamumugene sulseparvovec | Metabolic Disorders |
LYSOGENE | olenasufligene relduparvovec | Metabolic Disorders |
MADRIGAL PHARMACEUTICALS | resmetirom | Metabolic Disorders |
METACRINE | omesdafexor | Metabolic Disorders |
MILLENDO | livoletide | Metabolic Disorders |
NGM BIOPHARMACEUTICALS | aldafermin | Metabolic Disorders |
NOVO NORDISK | somapacitan | Metabolic Disorders |
ORCHARD THERAPEUTICS | azamidugene autotemcel | Metabolic Disorders |
ORIGIN BIOSCIENCES | fosdenopterine | Metabolic Disorders |
ORPHALAN | trientine tetrahydrochloride | Metabolic Disorders |
ORPHAN TECHNOLOGIES | pegtibatinase | Metabolic Disorders |
PFIZER | clesacostat | Metabolic Disorders |
PFIZER | ervogastat | Metabolic Disorders |
PFIZER | lotiglipron | Metabolic Disorders |
PTC THERAPEUTICS | UPSTAZA | Metabolic disorders |
REGENERON | rapirosiran | Metabolic Disorders |
REGENERON | rapirosiran sodium | Metabolic Disorders |
REMD BIOTHERAPEUTICS | volagidemab | Metabolic Disorders |
REMD BIOTHERAPEUTICS | volagidemab | Metabolic Disorders |
SAGIMET | denifanstat | Metabolic Disorders |
SANGAMO | isaralgagene civaparvovec | Metabolic Disorders |
SANGAMO THERAPEUTICS | devafidugene civaparvovec | Metabolic Disorders |
SANGAMO THERAPEUTICS | tefidsogene civaparvovec | Metabolic Disorders |
SCOHIA PHARMA | sucunamostat | metabolic disorders |
TAKEDA | maralixibat chloride | Metabolic Disorders |
TAKEDA | valanafusp alfa | Metabolic Disorders |
TAKEDA GLOBAL | KAPIDEX | Metabolic Disorders |
TAYSHA GENE THERAPIES | engabexagene cincesparvovec | Metabolic Disorders |
TEVA PHARMACEUTICAL INDUSTRIES | albusomatropin | Metabolic Disorders |
ULTRAGENYX | avalotcagene ontaparvovec | Metabolic Disorders |
ULTRAGENYX | rivunatpagene miziparvovec | Metabolic Disorders |
ULTRAGENYX | triheptanoin | Metabolic Disorders |
UNIQURE | GLYBERA | Metabolic Disorders |
VALERION THERAPEUTICS | clervonafusp alfa | Metabolic Disorders |
VERSARTIS | somavaratan | Metabolic Disorders |